FDA approves Pharming’s Joenja® as first treatment for children with APDS in the U.S.
Pharming Group N.V. announced FDA approval for its drug Joenja® (leniolisib) to treat children aged 4 to 11 years weighing at least 27 kg with activated phosphoinositide 3-kinase delta syndrome (APDS), a rare primary immunodeficiency. This marks the first FDA approved treatment for younger pediatric APDS patients in the U.S., expanding the indicati…