Beam Therapeutics Announces Compelling Updated Clinical Data from the Ongoing Phase 1/2 Trial of BEAM-302 in Alpha-1 Antitrypsin Deficiency (AATD) to Support Advancement to Pivotal Development
Beam Therapeutics announced updated clinical data from its ongoing Phase 1/2 trial of BEAM-302, a gene-editing therapy for Alpha-1 Antitrypsin Deficiency (AATD). The therapy showed a well-tolerated safety profile and durable increases in functional AAT protein with significant reduction in mutant Z-AAT after a single dose. Beam selected 60 mg as th…